You may qualify for the CHAMPIONS clinical research study if you:
  • Are at least 5 years old
  • Have MPS II
  • Are able and willing to use corticosteroids

People who qualify will receive:

  • Investigational gene therapy (SB-913) for MPS II
  • Study-related medical care
  • Reimbursement for travel (transportation assistance may be available)

Doctor with patient

To learn more about the study opportunity, please contact Contact Us
Find a Study Doctor

United States, California
UCSF Benioff Children’s Hospital Oakland
Oakland, California, United States, 94609
Contact: Jill Nicholas
510-428-3885 ext 5241
Principal Investigator: Paul Harmatz, MD

United States, Illinois
Ann & Robert H. Lurie Children’s Hospital of Chicago
Chicago, Illinois, United States, 60611
Contact: Carolyn Ries
Contact: Rachel Katz
Principal Investigator: Barbara Burton, MD

United States, North Carolina
University of North Carolina
Chapel Hill, North Carolina, United States, 27514
Contact: Heather Preiss, RN
Principal Investigator: Joesph Muenzer, MD

United States, Pennsylvania
Children’s Hospital of Philadelphia
Philadelphia, Pennsylvania, United States, 19104
Contact: Genevieve Nesom
Principal Investigator: Can Ficicioglu, MD

United States, Minnesota
University of Minnesota
Minneapolis, Minnesota, United States, 55455
Contact: Patricia Grover
Principal Investigator: Chester Whitley, MD, PhD

United States, New York
New York University School of Medicine
New York, NY, United States, 10016
Contact: Sara Rodriguez
Principal Investigator: Heather Lau, MD

United States, Ohio
Cincinnati Children’s Hospital Medical Center
Cincinnati, Ohio, United States, 45229
Contact: Laurie Bailey
Principal Investigator: Carlos E Prada, MD

Think the CHAMPIONS study may be for you?

Find a Study Doctor